Researchers combine gene therapy with optogenetics to curb abnormal neural activity and prevent seizure-like activity in neurons.

The U.S. Food and Drug Administration approved PTC Therapeutics, Inc.'s Kebilidi (eladocagene exuparvovec-tneq) gene therapy for the ...

The U.S. Food and Drug Administration approved Kebilidi (eladocagene exuparvovec-tneq), an adeno-associated virus ...

First-ever FDA approval for gene therapy directly administered to the brain - - Priority review voucher granted - - Broad label including children and adults - - ...

This is the first gene therapy for AADC deficiency to receive US regulatory approval and the first that can be administered directly to the brain.

WARREN, NJ, USA I November 13, 2024 I PTC Therapeutics, Inc. (NASDAQ: PTCT) announced today the U.S. Food and Drug Administration (FDA) accelerated approval of its gene therapy for the treatment of ...

Evidence of as many as 20 human skulls was located in New Mexico property after a witness gave a ride to had an “unsettling encounter” with a man he offered a ride. Lea County Sheriff’s ...

As many as 20 human skulls were found in a New Mexico home after the man who lived there tossed bones out of a car while hitching a ride, according to police. Police made the grisly discovery ...

Law enforcement officials in Jal, New Mexico, are investigating the discovery of multiple human skulls, including one that authorities have connected to a woman's disappearance in 2019.

Up to 20 human skulls have been found in a home in New Mexico, and police believe that one of them may be connected to a woman’s disappearance more than five years ago. The Lea County Sheriff ...

By Michael Levenson Fragments of 10 to 20 human skulls have been discovered in a burned-out house in a small town in New Mexico, raising unsettling questions about who the bones belonged to and ...